Key Sessions
Laura Sepp-Lorenzino, PhD
Presentation: Advancing Genome and RNA Editing for Precision Medicine
GNMmeds LLC
Karina Thorn
Panel: RNA Drug Discovery - Fostering the Next Wave of RNA Medicines
Novo Nordisk
Shaan Gandhi
Panel: Funding and Partnerships Dynamics in Genetic Medicines
Pfizer
Friday, September 25 - EST (Eastern Time, UTC-05:00
Friday, September 25 - EST (Eastern Time, UTC-05:00
8:00am - 9:00am60 mins
Registration
9:00am - 9:25am25 mins
Oligo-based Therapeutics: ASOs Clinical Advancements
Development and progression to the clinic of antisense oligonucleotide to advance treatment of ALS and FTD
9:00am - 9:25am25 mins
mRNA & Next-Gen RNA: Non-Linear Innovation
Advancing circRNA expression systems applied to in vivo CAR cell Therapy
- Lubor Gaal - CFO, Circio AB
9:25am - 9:50am25 mins
Oligo-based Therapeutics: ASOs Clinical Advancements
Phase 1a Clinical Trial of TTX-MC138, a First-in-Class Antagomir against Advanced Solid Tumors
- Zdravka Medarova, PhD - Co-Founder and Chief Scientific Officer, TransCode Therapeutics
9:25am - 9:50am25 mins
mRNA & Next-Gen RNA: Non-Linear Innovation
In Vivo CAR T with RNA Medicines for Scalable and Safe Immune Cell Reprogramming
- Michael Lam - VP Strategic & Scientific External Affairs, Sail Biomedicines
9:50am - 10:15am25 mins
Oligo-based Therapeutics: ASOs Clinical Advancements
Innovating Oligonucleotide Production: Chemoenzymatic Synthesis
- Wuming Yan - Chief Scientist Oligonucleotides, Asymchem
9:50am - 10:15am25 mins
mRNA & Next-Gen RNA: Non-Linear Innovation
Harnessing circRNA therapeutics for durable and tolerable treatments in oncology and autoimmune diseases - Preclinical Updates
- Peter Weinstein - CEO, Circurna
10:15am - 11:20am65 mins
Partnering Hour
11:20am - 11:45am25 mins
Oligo-based Therapeutics: siRNA Clinical Advancements
Advancing PGN-EDODM1, an enhanced peptide for clinical studies to treat DMD1
- Jane Larkindale - VP Clinical Science, PepGen Inc.
11:20am - 11:45am25 mins
mRNA & Next-Gen RNA: Clinical Advancements
Advancing tRNA Therapeutics for Stop Codon Disease: Preclinical Data Supporting a Basket Clinical Development Strategy
11:45am - 12:10pm25 mins
Oligo-based Therapeutics: siRNA Clinical Advancements
Clinical Translation of SGB-7342 - Design and Implementation RNAi Therapy for Metabolic Disease
- Weimin Wang, PhD - Founder & CEO, Sanegene Bio
11:45am - 12:10pm25 mins
mRNA & Next-Gen RNA: Clinical Advancements
Advancing mRNA Therapeutics with Strand Signal Stack
- Tasuku Kitada - President and Head of R&D, Strand Therapeutics
12:10pm - 12:35pm25 mins
Oligo-based Therapeutics: siRNA Clinical Advancements
Advancing siRNA Manufacture From Conventional to Thermostable Enzymatic Ligation
- Xiaocen (Chris) Li, PhD - Director of Oligonucleotide Science and Technology, Hongene
12:10pm - 12:35pm25 mins
mRNA & Next-Gen RNA: Clinical Advancements
Advancing Therapeutic Angiogenesis: First-in-Human Trial of HM2002 Circular RNA Therapy for Ischemic Heart Failure in CABG Patients
12:35pm - 2:00pm85 mins
Lunch
2:00pm - 2:30pm30 mins
Keynote Session
Presentation: Advancing Genome and RNA Editing for Precision Medicine
- Laura Sepp-Lorenzino, PhD - Biotech Executive, Board Member and Industry Advisor, GNMmeds LLC
2:30pm - 3:15pm45 mins
Keynote Session
Panel: RNA Drug Discovery - Fostering the Next Wave of RNA Medicines
- Karina Thorn - Vice President, Head of Nucleic Acid Research, Novo Nordisk
- Laura Sepp-Lorenzino, PhD - Biotech Executive, Board Member and Industry Advisor, GNMmeds LLC
- Muthiah (Mano) Manoharan, PhD - Senior Vice President of Drug Innovation and Distinguished Research Scientist, Alnylam Pharmaceuticals
- Malgorzata Gonciarz - Global Head xRNA Therapeutics, Novartis
3:15pm - 4:00pm45 mins
Keynote Session
Panel: Funding and Partnerships Dynamics in Genetic Medicines
- Shaan Gandhi - VP and Head of Partnerships, PAVE, Pfizer
- Elena Diez Cecilia - Senior Director External Innovation DPDS, Johnson & Johnson
- Soyoung Park - General Partner, 1004 Venture Partners
4:00pm - 4:15pm15 mins
Keynote Session
Closing Remarks
- Jade Osei-Tutu - Head of RNA Leaders, Informa Connect
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