Key Sessions
Malgorzata Gonciarz
Presentation: Utilising External Innovation pathways for accelerated clinical transition of RNA Therapies
Novartis
Anders Näär
Panel: The role of AI in RNA - Drug Discovery, Rare Diseases and Clinical Applications
UC Berkeley
Presentation: Exploring mRNA/next-gen RNA routes for future market success
Bao Cai, PhD
Panel: Scaling RNA Manufacturing
Sarepta Therapeutics
Chandra Vargeese, PhD
Presentation: RNAi Targeting INHBE for Obesity and Metabolic Disorders: Genetic Validation, Mechanism, and Clinical Translation
Wave Life Science
Derek Gauntlett
Presentation: Advanced Ligation and Stereochemical Control for Scalable RNA Manufacturing
Codexis
Presentation: Nanoparticles for Tissue-Targeted RNA Delivery: From Library Design to In Vivo

