Main Conference - Day 3 (May 14)
6:45am - 7:45am60 mins
Sunrise Yoga
Sunrise Yoga: Wellness Event - Reservation Required
7:15am - 7:45am30 mins
Registration
Registration
Breakfast Spotlight Presentations
7:45am - 8:15am30 mins
Breakfast Spotlight Presentations 1
LNP-production for mRNA-vaccines, Therapeutics and for Gene-editing - Proof of Concept for a Versatile Process
- Thomas Vrucina - Deputy Head Liposome Technology, Polymun Scientific
Case Studies of Preclinical and Clinical Oligonucleotides in Development
8:25am - 8:30am5 mins
Oligonucleotide Discovery, Preclinical and Clinical
Chairwoman’s Remarks
8:25am - 8:30am5 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Chairman’s Remarks
- Seb Caille, PhD - Senior Director, Avidity Biosciences
8:25am - 8:30am5 mins
Peptide Discovery to CMC
Co-Chairs' Remarks
- Matteo Villain, PhD - Vice President of Peptide and Oligonucleotide, Veranova
- Marc Jacob, PhD - Head of Strategic Development, Chromatography Products, YMC America
8:25am - 8:30am5 mins
Genome Editing Technology and Applications
Co-Chairs' Remarks
8:25am - 8:30am5 mins
Delivery of Macromolecules
Chairwoman’s Remarks
8:30am - 9:00am30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
8:30am - 9:00am30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Controlling Phosphorothioate Stereochemistry: Challenges and Innovations in Oligonucleotide Manufacturing
- Stefan Lutz, PhD - Chief Scientific Officer, Codexis
8:30am - 9:00am30 mins
Peptide Discovery to CMC
Chemically Convergent Peptide Synthesis: Eliminating SPPS and the Impact on Registered Starting Material Designations
- Kevin Seibert, PhD - Vice President, Engineering, Synthetic Molecule Design and Development, Eli Lilly and Company
8:30am - 9:00am30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
8:30am - 9:00am30 mins
Delivery of Macromolecules
Systemic RNAi Targeting MAPT: Advancing Tau Suppression Across the CNS with TRiM™ SC
9:00am - 9:30am30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
9:00am - 9:30am30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Oligonucleotide CMC Case Study
9:00am - 9:30am30 mins
Peptide Discovery to CMC
Peptide CMC Case Study
9:00am - 9:30am30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
9:00am - 9:30am30 mins
Delivery of Macromolecules
Oleic Acid Conjugation as a Brain Shuttle to Reach Nervous System after IV Injection
- Beatriz De La Torre, Ph.D. - Research Professor, Laboratory of Medicine and Med, University Of KwaZulu-Natal
9:30am - 10:00am30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
9:30am - 10:00am30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Oligonucleotide CMC Case Study
9:30am - 10:00am30 mins
Peptide Discovery to CMC
CMC/Commercial Strategies for MK-0616
- Levi Knippel, Ph.D - Senior Scientist, Merck
9:30am - 10:00am30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
9:30am - 10:00am30 mins
Delivery of Macromolecules
Late Breaking Presentation
10:00am - 10:45am45 mins
Networking Refreshment Break in Poster and Exhibit Hall
10:45am - 11:15am30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
10:45am - 11:15am30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Presentation Title TBA
- Sandro Nalli, Ph.D - Vice President, Technical Development and Operation, Avidity Biosciences
10:45am - 11:15am30 mins
Peptide Discovery to CMC
GLP-1 API Manufacturing Under Pressure: Starting-Material and CDMO Challenges for Emerging Biotechs
- Pin-Nan Cheng, Ph.D - Sr Dir, Drug Substance Development, CMC, Altimmune
10:45am - 11:15am30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
10:45am - 11:15am30 mins
Delivery of Macromolecules
Late Breaking Presentation
11:15am - 11:45am30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
11:15am - 11:45am30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
CMC Perspectives and Lessons Learned from TAC-001
- Mark Karmarz, Ph.D - Executive Director of Biologics Development, Tallac Therapeutics
11:15am - 11:45am30 mins
Peptide Discovery to CMC
Peptide CMC Case Study
11:15am - 11:45am30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
11:15am - 11:45am30 mins
Delivery of Macromolecules
Late Breaking Presentation
11:45am - 12:15pm30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
11:45am - 12:15pm30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
FORCE Platform to Enable Delivery of Oligonucleotides for the Treatment of Neuromuscular Diseases
- Saul Martinez Montero - Senior Director and Head of Oligonucleotide Therapeutics, saul.mmontero@dyne-tx.com
11:45am - 12:15pm30 mins
Peptide Discovery to CMC
Comprehensive Characterization of Peptides and New Modalities Using Multidimensional Chromatography and Mass Spectrometry
- C. J. Venkatramani, PhD - Distinguished Scientist, Genentech
11:45am - 12:15pm30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
11:45am - 12:15pm30 mins
Delivery of Macromolecules
Late Breaking Presentation
12:15pm - 12:20pm5 mins
Oligonucleotide Discovery, Preclinical and Clinical
Transition to Spotlight Presentation Rooms
12:15pm - 12:20pm5 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Transition to Spotlight Presentation Rooms
12:15pm - 12:20pm5 mins
Peptide Discovery to CMC
Transition to Spotlight Presentation Rooms
12:15pm - 12:20pm5 mins
Genome Editing Technology and Applications
Transition to Spotlight Presentation Rooms
12:15pm - 12:20pm5 mins
Delivery of Macromolecules
Transition to Spotlight Presentation Rooms
12:20pm - 12:50pm30 mins
Spotlight Presentation 1
Tagging the Future: Scalable Biopolymer Production in Solution
- Matteo Villain, PhD - Vice President of Peptide and Oligonucleotide, Veranova
12:20pm - 12:50pm30 mins
Spotlight Presentation 4
Revolutionizing Gene Therapy through Non-Viral, Tissue-Selective Delivery Platforms
- Joo-Sung Yang - VP and Head of the New Therapeutics Business Development, Samyang Biopharm
12:20pm - 12:50pm30 mins
Spotlight Presentation 5
Efficient Conformational Sampling in Nucleic Acids Using LowModeMD
- Alain Deschênes - Vice President, Chemical Computing Group
12:50pm - 1:55pm65 mins
Networking Luncheon in Poster and Exhibit Hall
Networking Luncheon with Last Chance for Poster & Exhibit Viewing
1:10pm - 1:20pm10 mins
TIDES Talks in Poster and Exhibit Hall
TIDES Talk
1:20pm - 1:30pm10 mins
TIDES Talks in Poster and Exhibit Hall
TIDES Talk
1:55pm - 2:00pm5 mins
Oligonucleotide Discovery, Preclinical and Clinical
Chairman’s Remarks
1:55pm - 2:00pm5 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Chairwoman’s Remarks
- Lori Troup - Director of Analytical Development, Dicerna/Novo Nordisk
1:55pm - 2:00pm5 mins
Peptide-Oligonucleotide Conjugates
Chairman’s Remarks
- Elissa Hobert, PhD - Director of Discovery Technologies, NewCo
1:55pm - 2:00pm5 mins
Genome Editing Technology and Applications
Chairman’s Remark's
2:00pm - 2:30pm30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
2:00pm - 2:30pm30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Regulatory Expectations for Synthetic Oligonucleotides: Trends, Challenges, and Opportunities
- Katharine (Katie) Duncan, PhD - Director, CMC Policy and Advocacy, GlaxoSmithKline (GSK)
2:00pm - 2:30pm30 mins
Peptide-Oligonucleotide Conjugates
Novel Extrahepatic RNAi Therapeutics for Obesity Targeting Adipocytes and Skeletal Muscle via the LEAD™ Technology
- Marc Abrams, PhD - Chief Technology Officer & Head, US Operations, SanegeneBio
2:00pm - 2:30pm30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
2:30pm - 3:00pm30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
2:30pm - 3:00pm30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Practical Application of Platform Approaches for Oligonucleotides
- Jennifer Franklin - Executive Director, CMC Regulatory Affairs, Ionis Pharmaceuticals
2:30pm - 3:00pm30 mins
Peptide-Oligonucleotide Conjugates
The Strike Platform Enables Kidney-Selective Gene Silencing
- Mangala Soundar - VP Biology, Judo Bio
2:30pm - 3:00pm30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
3:00pm - 3:30pm30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
3:00pm - 3:30pm30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Application of Accelerated Predictive Stability to siRNA Long Term Stability Assessment
- Zhichao Zhang, Ph.D - Advisor, Bioproduct Research and Development, Eli Lilly & Company
- Shayak Samaddar, Ph.D - Senior Advisor, Drug Product Formulation, Eli Lilly & Company
3:00pm - 3:30pm30 mins
Peptide-Oligonucleotide Conjugates
siRNA CNS Delivery Using Peptide Ligands and Preclinical Development
- Lucas Siow - CEO and Co-Founder, ProteinQure
3:00pm - 3:30pm30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
3:30pm - 4:00pm30 mins
Networking Refreshment Break
4:00pm - 4:30pm30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
4:00pm - 4:30pm30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
A Risk-Based Framework for Microbiological Control in Oligonucleotide Drug Substance Manufacturing
- Bharath Venkatram - Senior Engineer, Process Development & Scale Up La, Amgen
4:00pm - 4:30pm30 mins
Peptide-Oligonucleotide Conjugates
Amphiphilic Shuttle Peptide Enables the Development of PMO-based Therapeutics to Treat Basal Cell Carcinoma and Muco-obstructive Lung Diseases
- David Guay, PhD - VP Innovation & Technology, Feldan Therapeutics
4:00pm - 4:30pm30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
4:30pm - 5:00pm30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
4:30pm - 5:00pm30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Ensuring Diastereomeric Consistency in Phosphorothioate-modified siRNAs: Analytical and Process Strategies for Robust Clinical Development
- Joanna Hemming Taylor, PhD - Associate Principal Scientist, AstraZeneca
4:30pm - 5:00pm30 mins
Peptide-Oligonucleotide Conjugates
Delivering RNAi to Extra-hepatic Tissues
- Punit Seth, PhD - SVP, Research, Alnylam Pharmaceuticals
4:30pm - 5:00pm30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
5:00pm - 5:30pm30 mins
Oligonucleotide Discovery, Preclinical and Clinical
May 13/14 Agenda Coming Soon
5:00pm - 5:30pm30 mins
Oligonucleotide Chemistry, Manufacturing and Controls
Development of a HILIC-WAX Two-Dimensional Liquid Chromatography Method for UV-Based Quantitation of Antisense Oligonucleotide Impurities
- Xiao Zhou - Senior Scientist, Biogen
5:00pm - 5:05pm5 mins
Peptide-Oligonucleotide Conjugates
Discovery and Translation of Extrahepatic Peptides for Oligonucleotide Delivery
- Uyanga Tsedev - Founder & Chief Scientific Officer, Gensaic
5:00pm - 5:30pm30 mins
Genome Editing Technology and Applications
May 13/14 Agenda Coming Soon
5:30pm - 5:35pm5 mins
Close of TIDES 2026
* 不測の事態により、事前の予告なしにプログラムが変更される場合があります。